The STR1VE Trial of Onasemnogene Abeparvovec in SMA
Basil Darras, MD provides an overview of safety and efficacy data from the phase 3 STR1VE clinical trial of onasemnogene abeparvovec in patients with symptomatic SMA up to 6 months of age.
The START Trial of Onasemnogene Abeparvovec in SMA
Tom Crawford, MD provides key insights into the START clinical trial of onasemnogene abeparvovec in symptomatic SMA and discusses its safety and efficacy for children up to 24 months of age.
Advancements in Clinical Trial Design in ALS
A panel of experts provides insights into recent improvements in clinical trial design in amyotrophic lateral sclerosis (ALS) and discusses implications of recent clinical trial results.
Approaches to Pharmacologic Management of ALS
Expert neurologists discuss clinical trial design and FDA approvals for current approaches to pharmacologic management of amyotrophic lateral sclerosis (ALS) and share personal experiences.
Advantages of Sublingual Apomorphine in Parkinson Disease: Jennifer S. Hui, MD
May 17th 2021The assistant professor of neurology at the Keck School of Medicine at University of Southern California shared her insight into the study data and the therapy’s potential advantages for patients with Parkinson disease.