Onasemnogene Abeparvovec for the Treatment of SMA
Key opinion leader in neurology Carolina Tesi Rocha, MD provides an overview of onasemnogene abeparvovec by discussing its mechanism of action, safety, and efficacy for patients with SMA.
The NURTURE Trial of Nusinersen in SMA
Experts in neurology Tom Crawford, MD and Claudia Chiriboga, MD, MPH discuss the impact of the NURTURE trial of nusinersen in patients with presymptomatic SMA.
Challenges of Respiratory Care in Patients with ALS
Key opinion leaders consider the importance of respiratory care in ALS by discussing immunization against respiratory illness as well as the use of non-invasive ventilation.
Building a Dialogue on Life Sustaining Care in ALS
Panelists share approaches for building a dialogue on life sustaining care such as invasive ventilation and discuss the importance of social and cultural factors for patients and families.
Patient Conversations About Clinical Development in ALS: Matthew B. Harms, MD
May 10th 2021The associate professor of neurology at Columbia University and medical consultant and care center director at the Muscular Dystrophy Association spoke to the importance of staying up on the latest developments in ALS and keeping patients in the loop on that information.
The Impact of Big Data on ALS Care: Matthew B. Harms, MD
May 9th 2021The associate professor of neurology at Columbia University and medical consultant and care center director at the Muscular Dystrophy Association discussed the use of larger datasets to improve prognostication and clinical trials in ALS.