News
Timing of Treatment and Managing Attacks in MOGAD: Anastasia Vishnevetsky, MD
April 10th 2023The immunology fellow at Brigham and Women’s Hospital discussed the current state of care for patients with MOGAD, and whether treatment decisions differ based on timing of attacks. [WATCH TIME: 7 minutes]
Revolutionizing Treatment For Duchenne Muscular Dystrophy with Gene Editing: Courtney Young, PhD
April 10th 2023The co-founder and chief executive officer of MyoGene Bio talked about the advantages of gene editing over traditional gene therapy as a long term treatment for neuromuscular diseases at MDA’s 2023 conference. [WATCH TIME: 3 minutes]
Physical Therapy, Optimizing Function in Neuromuscular Diseases: Megan Iammarino, PT, DPT
April 9th 2023The research physical therapist at Nationwide Children’s Hospital talked about the role of physical therapy in the changing landscape of care with neuromuscular diseases at the 2023 MDA conference. [WATCH TIME: 5 minutes]
The Development of New Gene Therapies to Address Unmet Needs in ALS: Matthew B. Harms, MD
April 7th 2023The associate professor of neurology at Columbia University spoke at the 2023 MDA conference about the unmet needs of patients with ALS and the potential of new gene therapies. [WATCH TIME: 5 minutes]
Successes and Advances in Migraine Care Through Headache on the Hill: Julienne Verdi
April 6th 2023The executive director of the Alliance for Headache Disorders Advocacy discussed some of the successes from recent Headache on the Hills, and the expansion in centers of excellence for veterans with migraine. [WATCH TIME: 6 minutes]
Early Monitoring and Treatment for Bone Health in Duchenne Muscular Dystrophy: Meilan Rutter, MD
April 6th 2023At the 2023 MDA conference, a pediatric endocrinologist from Cincinnati Children’s Hospital talked about the unmet needs in treating bone health for patients with Duchenne muscular dystrophy. [WATCH TIME: 5 minutes]
Neflamapimod Demonstrates Positive Impact on Cholinergic Degenerative Process in Alzheimer Disease
April 6th 2023Treatment with neflamapimod was associated with statistically significantly higher functional dynamic connectivity, with almost half of the cohort experiencing a greater than 10% increase over time.
Building a Greater Understanding for NMOSD Treatments, Neurodegeneration: John Chen, MD, PhD
April 5th 2023The neuroophtalmologist at Mayo Clinic detailed improvements in prescribing methods for NMOSD treatments and the conversations surrounding reversing neurodegeneration. [WATCH TIME: 3 minutes]
Natural History of Rett Syndrome and Managing Adverse Events with Newly FDA-Approved Trofinetide
April 5th 2023Robin Ryther, MD, PhD, director of the Rett Spectrum Clinic at Washington University in St. Louis School of Medicine, shared her response to the recently approved therapy trofinetide for Rett syndrome.
Personalized Treatment Approaches of Myopathies Based on Antibodies: Suur Bilicier, MD
April 5th 2023The associate professor of neurology at the University of Texas Health Science Center at Houston talked about advances in the classification of inflammatory myopathies at the recently concluded 2023 MDA conference. [WATCH TIME: 4 minutes]
Reasons for the Complex Diagnosis of Basilar Artery Occlusions: Russell Cerejo, MD
April 5th 2023The vascular neurologist at Allegheny Health Network provided perspective on the complex diagnosis of basilar artery occlusions and the signs clinicians and emergency room specialists should be aware of. [WATCH TIME: 2 minutes]
Top Interviews from 2023 MDA: Expert Insights on Neuromuscular Diseases
April 4th 2023A group of experts in the care of patients with neuromuscular diseases—Douglas Sproule, MD, MSc; David Brumbaugh, MD; Sharon Hesterlee, PhD; Lauren Treat, MD; Donovan Lott, PT, PhD, CSCS—shared their perspectives on hot topics of treatment and management from the 2023 MDA conference.
