Opinion|Videos|July 3, 2024

Current and Emerging Treatment Options and Management of Duchenne Muscular Dystrophy

Author(s)Emma Ciafaloni, MD

An expert on Duchenne muscular dystrophy reviews standard-of-care treatment options and provides clinical insights on adverse effects and safety concerns, particularly with corticosteroids.

Video content above is prompted by the following questions:

Please briefly describe the current standard of care for Duchenne muscular dystrophy (DMD).
- What are the side effects and/or safety concerns associated with long-term use of corticosteroids in patients with DMD?
- Discuss recent approvals and ongoing studies in DMD.

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