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Videos

The autoimmune neurology program director at the University of Colorado talked about the emerging use of CAR T-cell therapy, a breakthrough from oncology, now being explored in autoimmune neurologic diseases like multiple sclerosis. [WATCH TIME: 3 minutes]

Paving the Way for Autoimmune Neurology Treatment With CAR T-Cell Therapy: Amanda Piquet, MD, FAAN

Articles

Take 5 minutes to catch up on NeurologyLive®'s highlights from the week ending February 28, 2025. 

NeurologyLive® Friday 5 — February 28, 2025

The vice president and senior global program lead for Hematology and Cell Therapy at BMS provided an overview behind the mechanism and early phase 1 data of BMS-986353 in various forms of multiple sclerosis. [WATCH TIME: 4 minutes]

Early Promise and Hypothesis Behind CAR T-Cell Therapy BMS-986353 in Multiple Sclerosis: Rosanna Ricafort, MD

Amber Freed, founder of SLC6A1 Connect, shared her personal journey and advocacy efforts to raise awareness for SLC6A1, a rare genetic epilepsy, in honor of Rare Disease Day.

Rare Disease Day 2025: Transforming Challenges Into Action for SLC6A1

Marco Meglio, Assistant Managing Editor for 

, has been with the team since October 2019. Follow him on Twitter 

Staff neurologist, Mellen Center for Multiple Sclerosis Treatment and Research, Cleveland Clinic

The staff neurologist at the Mellen Center for Multiple Sclerosis at Cleveland Clinic discussed how the CALLIPER trial’s lower proportion of patients with gadolinium-enhancing lesions mirrors clinical practice more closely than other progressive MS trials. [WATCH TIME: 2 minutes]

Ways to Align Patient Characteristics of Progressive Multiple Sclerosis Trials With Clinical Reality: Robert J. Fox, MD

Mary Schroth, MD, FAAP, FCCP, chief medical officer at Cure SMA, shed insight on the advances and promise for treating spinal muscular atrophy, in the context of Rare Disease Day.

Rare Disease Stories of Success: Newfound Hope for Spinal Muscular Atrophy

The staff neurologist at the Mellen Center for Multiple Sclerosis at Cleveland Clinic discussed key insights into patient characteristics and lesion differences of the CALLIPER Trial in retrospect to other studies. [WATCH TIME: 4 minutes]

Insights on Baseline Characteristics From Major Clinical Trials in Progressive Multiple Sclerosis: Robert J. Fox, MD

NeurologyLive is your direct connection to the latest neurology news and interviews with expert neurologists in multimedia formats.

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Evolving Treatment Landscape of Duchenne Muscular Dystrophy

Emma Ciafaloni, MD, addresses the important role of multidisciplinary care in the treatment of patients with Duchenne muscular dystrophy.

Multidisciplinary Care in Duchenne Muscular Dystrophy

Video content above is prompted by the following question:

What suggestions do you have to navigate diagnosis and management of DMD and the role multidisciplinary teams can play throughout a patient’s journey?

Emma Ciafaloni, MD, provides comprehensive insights on the treatment of Duchenne muscular dystrophy, focusing on diagnostic and treatment practices, ongoing research, and the importance of multidisciplinary care.

Emma Ciafaloni, MD, provides an overview of the clinical presentation and diagnosis of Duchenne muscular dystrophy (DMD), highlighting the role of CK testing and the pathophysiology of the disorder.

Clinical Presentation and Diagnosis of Duchenne Muscular Dystrophy

A neurology specialist offers clinical insights on communicating with patients about the diagnosis of Duchenne muscular dystrophy and discusses the important role of neuromuscular disease specialists.

Communication of Duchenne Muscular Dystrophy Diagnosis and Coordination of Care

An expert on Duchenne muscular dystrophy reviews standard-of-care treatment options and provides clinical insights on adverse effects and safety concerns, particularly with corticosteroids.

Current and Emerging Treatment Options and Management of Duchenne Muscular Dystrophy

Focusing on gene therapy and exon skipping medications, an expert on Duchenne muscular dystrophy discusses current and emerging treatment options.

Gene Therapy for Treatment of Duchenne Muscular Dystrophy

Emma Ciafaloni, MD, discusses therapies for Duchenne muscular dystrophy that target pathways downstream of dystrophin, focusing on vamorolone and givinostat.

Targeting Pathways Downstream of Dystrophin: Vamorolone and Givinostat in Duchenne Muscular Dystrophy

A neurologist discusses how recent approvals of therapies for Duchenne muscular dystrophy have improved patient outcomes.

Improvement in Management of Duchenne Muscular Dystrophy in Recent Years

Clinical

Lasso - DMD Peers and Perspectives NSP-21-NRD0157

 video series brings together pairs of expert clinicians and physicians to independently provide their insights on the latest and most up-to-date clinical care for specific neurologic diseases and disorders.

Multidisciplinary Care in Duchenne Muscular Dystrophy

EP: 1.Clinical Presentation and Diagnosis of Duchenne Muscular Dystrophy

EP: 2.Communication of Duchenne Muscular Dystrophy Diagnosis and Coordination of Care

EP: 3.Current and Emerging Treatment Options and Management of Duchenne Muscular Dystrophy

EP: 4.Gene Therapy for Treatment of Duchenne Muscular Dystrophy

EP: 5.Targeting Pathways Downstream of Dystrophin: Vamorolone and Givinostat in Duchenne Muscular Dystrophy

EP: 6.Improvement in Management of Duchenne Muscular Dystrophy in Recent Years

EP: 7.Multidisciplinary Care in Duchenne Muscular Dystrophy