Opinion

Video

Real-World Data for Risdiplam in Adult Patients with Spinal Muscular Atrophy

Panelists examine the available real-world data (RWD) on the use of risdiplam in adult patients with spinal muscular atrophy (SMA) from various studies conducted worldwide, discussing its potential efficacy and safety as a treatment option for adult SMA patients.

Related Videos
Stewart Tepper, MD
Richard B. Lipton, MD
Rita Perlingeiro, PhD
 J Mocco, MD, MS
Sheryll Baltazar, NP-C
Heather Medlin, MSW
© 2025 MJH Life Sciences

All rights reserved.